What is Duchenne Muscular Dystrophy (DMD)?
- DMD is the most common and most fatal form of muscular dystrophy
- Affects 1 in 3,500 boys; more than 20,000 in the US
- Rapidly damages voluntary muscles
- Prevents regeneration of damaged muscle cells
- Causes progressive muscle weakness, often confining boys aged ten and twelve to wheelchairs
- Exhausts children’s bodies of their ability to generate new cells
- Eventually results in paralysis, inability to breathe without assistance
- Most DMD children die in their early 20s
DMD is 100% Fatal – but it doesn’t have to be.
Together we can save lives!
“New therapeutic approaches are being discovered which “could transform this severely debilitating and lethal disease into a manageable chronic condition.” -Dr. M. Rudnicki, Ottowa Hospital Research Institute, June 2016.
This debilitating disorder is characterized by progressive muscle degeneration and weakness, as illustrated in the video above, “The Duchenne Timeline.” Current treatments represent the failure of 40 years of misplaced reliance on the drug research system. However, ground-breaking research in stem cell therapies, gene editing, and cell mobilizing therapies, some currently in use in many countries, are WORKING.